Lexeo Therapeutics Receives FDA Regenerative Medicine Advanced Therapy (RMAT) Designation for LX2020 for the Treatment of PKP2 Arrhythmogenic Cardiomyopathy
Lexeo Therapeutics received FDA Regenerative Medicine Advanced Therapy (RMAT) designation for LX2020, an investigational gene therapy for PKP2-associated arrhythmogenic cardiomyopathy. The designation was granted based on interim data from the ongoing HEROIC-PKP2 Phase I/II clinical trial, marking the third FDA designation for LX2020 alongside Orphan Drug and Fast Track status. PKP2 mutations affect approximately 60,000 people in the U.S.
Key figures
- Drug Name
- LX2020
- Phase Of Trial
- Phase I/II
- Affected population us
- approximately 60,000
- Pkp2 acm cases percentage
- approximately 50%
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