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PTC THERAPEUTICS, INC. (PTCT)

PTC Therapeutics, Inc. (PTCT) is a biopharmaceutical company committed to the research, development, and commercialization of innovative therapies for patients afflicted with rare genetic disorders. Its robust pipeline encompasses both commercialized therapies and a variety of experimental drug candidates, spanning all stages of development—from early research and preclinical studies to clinical trials—with a primary focus on addressing various rare disease indications. Among its commercialized products, PTC Therapeutics provides Translarna and Emflaza, offering therapeutic options for Duchenne muscular dystrophy patients in the European Economic Area and the United States. Translarna also addresses nonsense mutation Duchenne muscular dystrophy in Brazil and Russia. The company additionally commercializes Tegsedi and Waylivra for various rare conditions throughout Latin America and the Caribbean. Furthermore, in Brazil, PTC Therapeutics distributes Evrysdi as a treatment for spinal muscular atrophy (SMA) in patients aged two months and older. Leveraging its proprietary splicing platform, the company is also actively developing PTC518, a promising therapeutic candidate aimed at treating Huntington's disease. To bolster its research and development capabilities, PTC Therapeutics has established strategic collaborations, including partnerships with F. Hoffman-La Roche Ltd and Hoffman-La Roche Inc., as well as the Spinal Muscular Atrophy Foundation, focusing on advancing drug discovery and development research, particularly in regenerative medicine. Additionally, it collaborates with Akcea Therapeutics, Inc. for the commercialization of Tegsedi and Waylivra in the Latin America and Caribbean region. Established in 1998, PTC Therapeutics, Inc. maintains its corporate headquarters in South Plainfield, New Jersey.

Sector: Pharmaceutical Preparations

Industry: Biotechnology

PTC Therapeutics, Inc. logo

PTC Therapeutics, Inc.

NASDAQ:PTCTHealthcare
-6.97%$59.97
AH$61.55+2.63%vs close
Mkt Cap$5.01B
Float79.27M
O/S83.54M
Vol
$ Vol
RVOL
Inst Own-
SI10.5%
Earnings
Dilution
Financials Summary
Revenue$1.73B
Net Income$682.64M
Total Assets$2.9B
Free Cash Flow$411.18M
Debt & Equity
Debt 108%
Total Debt$2.71B
Total Equity-$205.31M
Shares Outstanding
Short Interest
Split History

No splits on record

Nothing in PTCT's public trading history: no forward or reverse split has affected the share count.

Balance Sheet Details
Assets$2.9B
Liabilities$3.1B
Accounts Receivable$181.62M
Accounts Payable$45.49M
Inventory$79.65M
PP&E (Net)$135.42M
Goodwill$82.34M
Intangible Assets$388.75M
Income Statement
PeriodFY 2025FY 2024FY 2023FY 2022FY 2021FY 2020FY 2019FY 2018FY 2017FY 2016FY 2015FY 2014FY 2013FY 2012FY 2011
CurrencyUSDUSDUSDUSDUSDUSDUSDUSDUSDUSDUSDUSDUSDUSDUSD
Period Ending2025-12-312024-12-312023-12-312022-12-312021-12-312020-12-312019-12-312018-12-312017-12-312016-12-312015-12-312014-12-312013-12-312012-12-312011-12-31
Revenue$1.73B$806.78M$937.82M$698.8M$538.59M$380.77M$306.98M$264.73M$194.39M$82.7M$36.77M$22.96M$31.33M$28.78M$98.96M
YoY Growth114.5%-14.0%34.2%29.7%41.4%24.0%16.0%36.2%135.0%124.9%60.1%-26.7%8.9%-70.9%-
Cost of Revenue$71.75M$57.4M$65.49M$44.68M$32.33M$18.94M$12.13M$12.67M$4.58M$117.63M$121.82M$79.84M$54.88M-$5.17M$0
Gross Profit$1.66B$749.38M$872.34M$654.12M$506.26M$361.82M$294.85M$252.06M$189.81M-$34.93M-$85.05M-$56.88M-$23.55M$33.95M$98.96M
Gross Margin95.9%92.9%93.0%93.6%94.0%95.0%96.0%95.2%97.6%-42.2%-231.3%-247.7%-75.2%118.0%100.0%
Research and Development$455.25M$534.48M$666.56M$651.5M$540.68M$477.64M$257.45M$171.98M$117.46M$117.63M$121.82M$79.84M$54.88M$46.14M$58.68M
Selling, General, and Administrative$347.14M$300.91M$332.54M$326M$285.77M$245.16M$202.54M$153.55M$121.27M$97.13M$82.08M$44.82M$25.22M$14.62M$16.15M
Other$0$216.56M$312.74M$124.04M$54.25M$70.78M$76.01M$129K-$1.28M-$1.21M-$465K-$213K$38K$1.78M$461K
Total Operating Expenses$802.39M$1.05B$1.31B$1.1B$880.71M$793.59M$536M$348.41M$254.11M$214.76M$203.9M$122.38M$76.72M$55.59M$68.38M
Operating Income (EBIT)$856.51M-$302.57M-$439.5M-$447.41M-$374.44M-$431.77M-$241.16M-$115.69M-$64.29M-$132.06M-$167.13M-$99.41M-$45.4M-$26.81M$30.58M
Operating Margin49.5%-37.5%-46.9%-64.0%-69.5%-113.4%-78.6%-43.7%-33.1%-159.7%-454.6%-432.9%-144.9%-93.2%30.9%
Interest Expense$152.23M$166.99M$129.18M$90.87M$86.02M$56.35M$12.49M$12.55M$12.09M$8.28M$2.37M$1.18M$6.08M$1.21M$2.44M
Interest Income$0$0$0$0$0$0$0$0$0$0$0$0$0$0$0
Other Income (Expense)-$159.89M-$60.55M-$256.61M-$140.08M-$143.9M$28.84M$1.23M-$12.43M-$13.37M-$9.48M-$2.83M$967K-$6.18M$573K-$1.98M
Income Before Tax (EBT)$696.62M-$363.12M-$696.11M-$587.49M-$518.34M-$402.93M-$239.93M-$128.11M-$77.67M-$141.54M-$169.96M-$98.45M-$51.57M-$26.24M$28.6M
Income Tax Expense$13.97M$176K-$69.51M-$28.47M$5.56M$35.23M$11.65M-$29K$1.33M$569K$485K-$4.69M$6.21M$1.21M-$2.31M
Net Income$682.64M-$363.3M-$626.6M-$559.02M-$523.9M-$438.16M-$251.58M-$128.08M-$79M-$142.11M-$170.45M-$93.75M-$51.57M-$26.24M$30.9M
Net Income Margin39.4%-45.0%-66.8%-80.0%-97.3%-115.1%-82.0%-48.4%-40.6%-171.8%-463.6%-408.3%-164.6%-91.2%31.2%
Supplementary Data
EPS8.58-4.73-8.37-7.79-7.43-6.64-4.27-2.75-2.02-4.17-5.07-2.97-4.02-1.850.00
Diluted EPS7.78-4.73-8.37-7.79-7.43-6.64-4.27-2.75-2.02-4.17-5.07-2.97-4.02-1.110.00
Weighted Average OS79.53M76.85M74.84M71.73M70.47M66.03M58.86M46.58M39.11M34.04M33.62M31.57M12.82M14.19M14.19M
EBITDA$887.66M-$120.46M-$330.34M-$367.78M-$368.18M-$303.09M-$195.25M-$89.47M-$46.61M-$128.77M-$164.25M-$97.18M-$43M-$24.1M$33.45M
EBITDA Margin51.3%-14.9%-35.2%-52.6%-68.4%-79.6%-63.6%-33.8%-24.0%-155.7%-446.8%-423.2%-137.3%-83.8%33.8%
Balance Sheet
PeriodFY 2025FY 2024FY 2023FY 2022FY 2021FY 2020FY 2019FY 2018FY 2017FY 2016FY 2015FY 2014FY 2013FY 2012FY 2011
CurrencyUSDUSDUSDUSDUSDUSDUSDUSDUSDUSDUSDUSDUSDUSDUSD
Period Ending2025-12-312024-12-312023-12-312022-12-312021-12-312020-12-312019-12-312018-12-312017-12-312016-12-312015-12-312014-12-312013-12-312012-12-312011-12-31
Assets
Current Assets
Cash and Cash Equivalents$984.65M$779.71M$594M$279.83M$189.72M$208.81M$288.03M$227.59M$191.25M$231.67M$338.93M$315.24M$15.41M$2.73M$28.43M
Short-Term Investments$960.72M$359.99M$282.74M$130.87M$583.66M$894.84M$398.54M$0$0$0$0$0$127.05M$0$0
Cash and Short-Term Investments$1.95B$1.14B$876.74M$410.7M$773.38M$1.1B$686.56M$227.59M$191.25M$231.67M$338.93M$315.24M$142.47M$2.73M$28.43M
Accounts Receivable$181.62M$158.55M$160.82M$155.61M$110.45M$69.93M$55.54M$67.91M$40.39M$24.93M$11.09M$4.45M$958K$1.01M$1.24M
Inventory$79.65M$23.19M$30.58M$21.81M$15.86M$18.7M$19.29M$16.12M$10.75M$0$0$0$0$0$0
Other Current Assets$67.31M$44.09M$150.49M$105.66M$0$0$0$9.25M$6.67M$4.69M$5.93M$3.88M$0$0$0
Total Current Assets$2.27B$1.37B$1.22B$693.78M$954.37M$1.23B$779.28M$320.86M$249.06M$261.29M$355.95M$323.57M$145.02M$4.6M$33.05M
Long-Term Assets
Property, Plant & Equipment Net$135.42M$117.66M$178.99M$175.02M$130.01M$118.24M$35.24M$12.69M$8.38M$7.43M$8.97M$9.16M$6.73M$8.28M$10.8M
Goodwill$82.34M$82.34M$82.34M$82.34M$82.34M$82.34M$82.34M$82.34M$0$0$0$0$0$0$0
Intangible Assets$388.75M$118.79M$379.5M$705.89M$724.84M$715.33M$710.5M$701.03M$132.99M$0$0$0$0$0$0
Long-Term Investments$0$0$0$0$0$0$0$0$0$0$0$0$0$0$0
Deferred Tax Assets$0$0$0$0$0$0$0$0$0$0$0$0$0$0$0
Other Long-Term Assets$18.3M$20.7M$36.25M$48.58M$46.5M$60.62M$16.41M$2.3M$1.22M$630K$3.12M$489K$149K$197K$298K
Total Long-Term Assets$624.82M$339.49M$677.07M$1.01B$983.69M$976.53M$844.5M$798.37M$142.59M$8.06M$12.09M$9.65M$6.88M$8.48M$11.09M
Other Assets$0$0$0$0$0$0$0$0$0$0$0$0$0$0$0
Total Assets$2.9B$1.71B$1.9B$1.71B$1.94B$2.21B$1.62B$1.12B$391.65M$269.35M$368.04M$333.22M$151.9M$13.07M$44.15M
Liabilities
Current Liabilities
Accounts Payable$45.49M$17.27M$6.04M$27.27M$23.03M$18.66M$10.32M$6M$15.28M$6.3M$5.78M$4.13M$1.12M$622K$1.88M
Short-Term Debt$569.63M$257.82M$194.31M$72.15M$208.83M$0$20M$11.67M$0$0$0$0$49K$4.44M$7.14M
Current Income Tax Payable$0$4.7M$0$4.71M$1.29M$4.32M$499K$0$0$0$0$0$0$0$0
Current Unearned Revenue$2.04M$5.5M$801K$1.35M$0$4.15M$8.24M$3.72M$3.94M$1.59M$139K$3.35M$877K$16.69M$22.96M
Other Current Liabilities$202.93M$120.22M$139.82M$126.46M$118.86M$129.89M$120.16M$117.78M$45.12M$29.68M$26.84M$15.68M$5.98M$3.1M$3.49M
Total Current Liabilities$968.43M$580.98M$603.1M$406.24M$509.35M$277.33M$235.86M$166.8M$82.05M$49.62M$45.39M$32.48M$13.13M$28.16M$43.15M
Long-Term Liabilities
Long-Term Debt$2.03B$2.11B$1.9B$1.26B$956.59M$309.14M$293.86M$141.35M$144.97M$98.22M$91.85M$0$0$439K$4.55M
Long-Term Unearned Revenue$0$0$0$0$0$0$3.42M$13.44M$11.89M$1.59M$139K$3.35M$0$742K$16.45M
Long-Term Deferred Tax Liabilities$0$0$55.91M$102.83M$137.11M$136.74M$130.86M$122.03M-$3.94M$0-$139K$0$0$378K$214.38M
Other Long-Term Liabilities$13.7M$22.23M$36.44M$166.64M$239.9M$900.53M$356.44M$328.6M$243K$335K$2.05M$2.28M$2.23M$2.55M$4.23M
Total Long-Term Liabilities$2.14B$2.22B$2.11B$1.65B$1.43B$1.45B$793.6M$601.7M$153.17M$100.14M$96.65M$2.28M$2.23M$4.11M$239.61M
Other Liabilities$0$0$0$0$0$0$0$0$0$0-$72.47M$0$0$0$0
Total Liabilities$3.1B$2.8B$2.71B$2.05B$1.94B$1.73B$1.03B$768.5M$235.22M$149.76M$69.57M$34.75M$15.36M$32.27M$282.75M
Stockholders' Equity
Preferred Stock$0$0$0$0$0$0$0$0$31K$485K$72.67M$0$151.9B$80.45M$0
Common Stock$80K$77K$75K$72K$71K$70K$62K$51K$42K$34K$34K$33K$24K$545$133
Retained Earnings-$2.96B-$3.65B-$3.28B-$2.66B-$2.1B-$1.63B-$1.19B-$938.92M-$814.11M-$735.11M-$593M-$422.55M-$328.8M-$277.22M-$250.61M
Comprehensive Income & Other$10.5M-$25.89M-$1.28M$4.8M-$24.28M-$60.96M-$10.58M$1.46M$3.97M-$1.49M-$1.2M-$737K$70K-$20.29M-$17.58M
Other Stockholders' Equity$2.76B$2.55B$2.46B$2.31B$2.1B$2.11B$1.78B$1.29B$970.5M$854.66M$891.43M$720.99M$465.32M$258.03M$12.01M
Total Equity-$205.31M-$1.1B-$818.55M-$347.09M$1.44M$481.98M$594.33M$350.73M$156.44M$119.58M$298.47M$298.47M$136.54M-$19.19M-$238.6M
Minority Interest$0$0$0$0$0$0$0$0$0$0$0$0$0$0$0
Total Liabilities and Equity$2.9B$1.71B$1.9B$1.71B$1.94B$2.21B$1.62B$1.12B$391.65M$269.35M$368.04M$333.22M$151.9M$13.07M$44.15M
Supplementary Data
Total Debt$2.71B$2.47B$2.23B$1.46B$1.27B$420.44M$328.03M$153.01M$144.97M$98.22M$94.61M$0$49K$4.88M$11.69M
Net Debt$1.72B$1.69B$1.64B$1.18B$1.08B$211.63M$40M-$74.57M-$46.27M-$133.45M-$244.32M-$315.24M-$15.37M$2.16M-$16.74M
Cash Flow Statement
PeriodFY 2025FY 2024FY 2023FY 2022FY 2021FY 2020FY 2019FY 2018FY 2017FY 2016FY 2015FY 2014FY 2013FY 2012FY 2011
CurrencyUSDUSDUSDUSDUSDUSDUSDUSDUSDUSDUSDUSDUSDUSDUSD
Period Ending2025-12-312024-12-312023-12-312022-12-312021-12-312020-12-312019-12-312018-12-312017-12-312016-12-312015-12-312014-12-312013-12-312012-12-312011-12-31
Operating Activities
Net Income$682.64M-$363.3M-$626.6M-$559.02M-$523.9M-$438.16M-$251.58M-$128.08M-$79M-$142.11M-$170.45M-$93.75M-$51.57M-$26.24M$30.9M
Depreciation & Amortization$38.81M$75.66M$236.59M$128.84M$64.13M$43.49M$32.18M$26.09M$17.68M$3.29M$2.88M$2.23M$2.4M$2.7M$2.87M
Deferred Income Tax-$3K-$55.91M-$46.93M-$34.28M$377K$5.87M$8.83M-$490K$199K-$199K$2.3M-$19.31M$92K-$1.78M-$462K
Stock-Based Compensation$74.55M$74.61M$131.21M$110.33M$103.51M$70.33M$42.13M$33.25M$30.56M$35.01M$33.98M$19.31M$8.43M$2.29M$2.82M
Changes in Working Capital:
  Accounts Receivable-$10.15M$1.73M-$1.54M-$48.47M-$44.99M-$10.48M$11.53M-$29.59M-$12.2M-$14.84M-$6.91M-$3.49M$56K$230K$0
  Inventory-$53.9M$6.16M-$8.18M-$6.67M$1.8M$1.84M-$3.46M-$5.82M-$6.45M$893K-$1.98M-$2.63M$0$0$0
  Accounts Payable$0$0$0$27.54M$23.41M$53.59M$13.75M$43.11M$24.01M$4.26M$16.98M$16.91M$5.18B$0$0
  Other Working Capital$16.17M$94.65M$5.72M-$57.74M-$4.01M-$8.03M-$1.39M$6.51M$7.87M$727K-$3.4M$2.4M-$5.2B-$25.13M-$57.31M
Total Working Capital Change-$47.88M$102.54M-$4M-$85.33M-$23.79M$36.91M$20.43M$14.21M$13.23M-$8.96M$4.7M$13.2M-$12.31M-$25.13M-$57.31M
Other Non-Cash Items-$36.93M$58.7M$151.32M$82.81M$128.33M$87.49M$49.37M$27.38M$7.27M$9.41M$2.25M$21.05M$6.05M$226K$417K
Net Cash from Operating$711.2M-$107.69M-$158.42M-$356.65M-$251.33M-$194.07M-$98.64M-$27.64M-$10.06M-$103.57M-$124.34M-$57.27M-$46.92M-$47.93M-$20.77M
Investing Activities
Capital Expenditures-$8.86M-$6.5M-$28.44M-$152.46M-$85.33M-$55.98M-$45.44M-$15.53M-$3.1M-$1.78M-$2.72M-$4.66M-$846K-$189K-$165K
Acquisitions$0$0$0$128.44M$57.12M$38.13M-$4M-$48.89M-$77.16M$0$0$0$0$0$0
Purchases of Investments-$1.42B-$667.36M-$212.48M-$75.55M-$543.27M-$1.45B-$494.07M-$68.61M-$81.37M-$85.38M-$223.76M-$247.8M-$156.04M$0-$2.02M
Sales of Investments$855.12M$607.74M$156.37M$518.19M$847.78M$944.09M$156.27M$90.42M$174.75M$191.63M$205.67M$107.3M$29.06M$0$29.89M
Other Investing Activities-$291.08M$110.31M-$92.18M-$128.44M-$57.12M-$38.13M$0$13.38M$16.22M$106.26M-$18.09M-$140.5M-$126.98M$0$0
Net Cash from Investing-$861.98M$44.18M-$176.74M$290.18M$219.18M-$561.55M-$387.24M-$42.61M$13.12M$104.48M-$20.81M-$145.17M-$127.83M-$189K$27.7M
Financing Activities
Debt Repaid$1.61M$1.49M$301.38M-$148.72M$2.22M$46.16M-$267.6M--$40M--$150M$49K$5M$6.94M$7.19M
Common Stock Issuance$99.05M$0$0$50M$23.1M$28.09M$323.76M$117.92M$2.47M$968K$8.71M$235.98M$131.65M$0$6K
Common Stock Repurchases$0$0$0$0$0$0$0$0$0$0$0$0$0$0$0
Dividends Paid$0$0$0$0$0$0$0$0$0$0$0$0$0$0$0
Other Financing Activities$233.66M$257.36M$947.78M-$30.77M$0$686.78M$21.85M$13.65M$4.22M$968K$4.06M$1.2M$51$0$0
Net Cash from Financing$331.09M$255.87M$646.4M$167.95M$20.88M$668.72M$613.21M$131.57M$44.22M$968K$154.06M$237.13M$187.44M$22.41M-$7.18M
Forex Effect$22.71M-$7.33M$3.11M-$2.77M-$7.82M$7.69M-$1.3M-$3.61M$6.2M-$1.58M-$639K-$350K$0$0$0
Net Change in Cash$203.02M$185.03M$314.36M$98.71M-$19.09M-$79.22M$126.03M$57.71M$53.47M$299K$8.27M$34.33M$12.69M-$25.71M-$243K
Supplementary Data
Operating Cash Flow$711.2M-$107.69M-$158.42M-$356.65M-$251.33M-$194.07M-$98.64M-$27.64M-$10.06M-$103.57M-$124.34M-$57.27M-$46.92M-$47.93M-$20.77M
Capital Expenditure-$300.01M-$74.25M-$120.62M-$152.46M-$85.33M-$55.98M-$45.44M-$15.53M-$3.1M-$1.78M-$2.72M-$4.66M-$846K-$189K-$165K
Free Cash Flow$411.18M-$181.94M-$279.04M-$509.11M-$336.66M-$250.05M-$144.08M-$43.17M-$13.16M-$105.34M-$127.06M-$61.94M-$47.77M-$48.12M-$20.93M
Cash at Beginning$795.32M$610.28M$295.93M$197.22M$216.31M$295.53M$169.5M$111.79M$58.32M$58.02M$49.75M$15.41M$2.73M$28.43M$28.67M
Cash at End$998.33M$795.32M$610.28M$295.93M$197.22M$216.31M$295.53M$169.5M$111.79M$58.32M$58.02M$49.75M$15.41M$2.73M$28.43M