REGENXBIO Inc. (RGNX)
REGENXBIO Inc. is a biotechnology company operating in the clinical stage, dedicated to developing gene therapy candidates. These therapies are designed to introduce genes into cells, aiming either to rectify genetic deficiencies or to stimulate the body's own cells to produce therapeutic proteins or antibodies to combat diseases. Central to its therapeutic development is the proprietary NAV Technology Platform, an adeno-associated virus-based gene delivery system. The company's primary investigational asset, RGX-314, is currently in Phase III clinical trials for treating wet age-related macular degeneration. Its pipeline also includes RGX-121 and RGX-111, both in Phase I/II trials for mucopolysaccharidosis type II and type I, respectively; RGX-181, which is in preclinical development for late-infantile neuronal ceroid lipofuscinosis type II disease; RGX-202, undergoing Phase I/II evaluation for Duchenne muscular dystrophy; and RGX-381, at the preclinical stage for addressing the ocular manifestations of CLN2 disease. In addition to its internal programs, REGENXBIO Inc. licenses its NAV Technology Platform to other biotech and pharmaceutical enterprises. It also maintains a collaborative and licensing agreement with Neurimmune AG for the advancement of innovative gene therapies. Founded in 2008, REGENXBIO Inc. maintains its headquarters in Rockville, Maryland.
Sector: Biological Products, (No Diagnostic Substances)
Industry: Biotechnology
REGENXBIO Inc.
No splits on record
Nothing in RGNX's public trading history: no forward or reverse split has affected the share count.
| Period | FY 2025 | FY 2024 | FY 2023 | FY 2022 | FY 2021 | FY 2020 | FY 2019 | FY 2018 | FY 2017 | FY 2016 | FY 2015 | FY 2014 | FY 2013 |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| Currency | USD | USD | USD | USD | USD | USD | USD | USD | USD | USD | USD | USD | USD |
| Period Ending | 2025-12-31 | 2024-12-31 | 2023-12-31 | 2022-12-31 | 2021-12-31 | 2020-12-31 | 2019-12-31 | 2018-12-31 | 2017-12-31 | 2016-12-31 | 2015-12-31 | 2014-12-31 | 2013-12-31 |
| Revenue | $170.44M | $83.33M | $90.24M | $112.72M | $470.35M | $154.57M | $35.23M | $218.5M | $10.39M | $4.59M | $7.59M | $6.12M | $6.09M |
| YoY Growth | 104.5% | -7.7% | -19.9% | -76.0% | 204.3% | 338.7% | -83.9% | 2002.4% | 126.5% | -39.5% | 24.0% | 0.5% | - |
| Cost of Revenue | $20.3M | $33.57M | $37.21M | $54.55M | $51.83M | $35.71M | $8.24M | $9.64M | $1.71M | $959K | $1.5M | $1.01M | $324K |
| Gross Profit | $150.14M | $49.76M | $53.03M | $58.18M | $418.51M | $118.85M | $26.99M | $208.87M | $8.68M | $3.63M | $6.08M | $5.11M | $5.76M |
| Gross Margin | 88.1% | 59.7% | 58.8% | 51.6% | 89.0% | 76.9% | 76.6% | 95.6% | 83.6% | 79.1% | 80.2% | 83.5% | 94.7% |
| Research and Development | $228.3M | $208.52M | $232.27M | $242.45M | $181.44M | $166.29M | $124.19M | $83.87M | $57.22M | $45.48M | $17.28M | $4.96M | $5.05M |
| Selling, General, and Administrative | $82.86M | $76.62M | $88.49M | $85.28M | $79.33M | $63.82M | $51.81M | $36.85M | $27.23M | $23.59M | $11.91M | $3.85M | $5.47M |
| Other | $179K | -$2.03M | $397K | -$6.68M | -$2.24M | $7.97M | -$10K | $42K | $116K | -$102K | -$26K | -$47K | $0 |
| Total Operating Expenses | $311.34M | $283.11M | $321.16M | $321.06M | $258.53M | $238.09M | $175.99M | $120.77M | $84.57M | $68.97M | $29.16M | $8.77M | $10.53M |
| Operating Income (EBIT) | -$161.2M | -$233.35M | -$268.13M | -$262.88M | $159.98M | -$119.23M | -$149M | $88.1M | -$75.89M | -$65.34M | -$23.14M | -$3.68M | -$4.78M |
| Operating Margin | -94.6% | -280.0% | -297.1% | -233.2% | 34.0% | -77.1% | -422.9% | 40.3% | -730.2% | -1423.8% | -304.9% | -60.2% | -78.5% |
| Interest Expense | $45.01M | $12.66M | $6.86M | $23.25M | $26.28M | $771K | $0 | $0 | $0 | $0 | $20K | $321K | $611K |
| Interest Income | $12.27M | $174K | $25K | $342K | $719K | $4.27M | $2.95M | $8.95M | $0 | $0 | $0 | $0 | $0 |
| Other Income (Expense) | -$32.68M | $6.24M | $4.48M | -$17.53M | -$18.73M | $13.22M | $51.51M | $16.02M | $2.72M | $1.94M | $326K | -$321K | -$611K |
| Income Before Tax (EBT) | -$193.88M | -$227.1M | -$263.65M | -$280.4M | $141.25M | -$106.01M | -$97.49M | $104.12M | -$73.17M | -$63.4M | -$22.81M | -$4M | -$5.39M |
| Income Tax Expense | $0 | $0 | -$152K | -$84K | $13.41M | $5.24M | -$2.75M | $4.18M | $686K | -$435K | -$60K | $0 | $0 |
| Net Income | -$193.88M | -$227.1M | -$263.49M | -$280.32M | $127.84M | -$111.25M | -$94.73M | $99.94M | -$73.17M | -$62.97M | -$22.81M | -$4M | -$5.39M |
| Net Income Margin | -113.8% | -272.5% | -292.0% | -248.7% | 27.2% | -72.0% | -268.9% | 45.7% | -704.0% | -1372.1% | -300.6% | -65.4% | -88.5% |
| Supplementary Data | |||||||||||||
| EPS | -3.76 | -4.59 | -6.02 | -6.50 | 3.01 | -2.98 | -2.58 | 2.73 | -2.45 | -2.38 | -2.49 | -0.30 | -2.04 |
| Diluted EPS | -3.76 | -4.59 | -6.02 | -6.50 | 2.91 | -2.98 | -2.58 | 2.73 | -2.45 | -2.38 | -2.49 | -0.30 | -2.04 |
| Weighted Average OS | 51.57M | 49.51M | 43.73M | 43.15M | 42.44M | 37.28M | 36.69M | 36.61M | 29.86M | 26.41M | 9.17M | 13.15M | 2.64M |
| EBITDA | -$133.25M | -$198.23M | -$239.46M | -$244.24M | $177.09M | -$96.83M | -$90.34M | $92.08M | -$73.2M | -$64.8M | -$22.71M | $0 | -$14K |
| EBITDA Margin | -78.2% | -237.9% | -265.4% | -216.7% | 37.7% | -62.6% | -256.4% | 42.1% | -704.3% | -1412.0% | -299.3% | - | -0.2% |
| Period | FY 2025 | FY 2024 | FY 2023 | FY 2022 | FY 2021 | FY 2020 | FY 2019 | FY 2018 | FY 2017 | FY 2016 | FY 2015 | FY 2014 | FY 2013 |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| Currency | USD | USD | USD | USD | USD | USD | USD | USD | USD | USD | USD | USD | USD |
| Period Ending | 2025-12-31 | 2024-12-31 | 2023-12-31 | 2022-12-31 | 2021-12-31 | 2020-12-31 | 2019-12-31 | 2018-12-31 | 2017-12-31 | 2016-12-31 | 2015-12-31 | 2014-12-31 | 2013-12-31 |
| Assets | |||||||||||||
| Current Assets | |||||||||||||
| Cash and Cash Equivalents | $34.47M | $57.53M | $34.52M | $96.95M | $345.21M | $338.43M | $69.51M | $75.56M | $46.66M | $24.84M | $54.12M | $1.12M | $1.12M |
| Short-Term Investments | $195.6M | $177.16M | $240.74M | $267.69M | $112.23M | $137.31M | $226.7M | $244.2M | $114.12M | $64.71M | $60.02M | $0 | $0 |
| Cash and Short-Term Investments | $230.07M | $234.69M | $275.26M | $364.64M | $457.44M | $475.74M | $296.21M | $319.76M | $160.78M | $89.55M | $114.14M | $1.12M | $1.12M |
| Accounts Receivable | $27.38M | $21.57M | $26.34M | $30.29M | $32.44M | $43M | $38.15M | $8.59M | $473K | $1.03M | $2.14M | $1.88M | $1.09M |
| Inventory | $0 | $0 | $0 | $0 | $0 | $10.51M | $0 | $5.73M | $5.33M | $1.77M | $1.02M | $0 | $0 |
| Other Current Assets | $11.9M | $12.68M | $18.85M | $7.14M | $10.2M | $1.95M | $4.2M | $3.83M | $1.41M | $1.01M | $851K | $0 | $0 |
| Total Current Assets | $281.28M | $278M | $334.97M | $415.98M | $518.83M | $531.2M | $345.03M | $337.91M | $168M | $93.37M | $118.15M | $3.03M | $2.21M |
| Long-Term Assets | |||||||||||||
| Property, Plant & Equipment Net | $152.01M | $171.31M | $192.59M | $206.8M | $192.45M | $120.28M | $39.05M | $28.7M | $13.98M | $9.32M | $538K | $0 | $0 |
| Goodwill | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 |
| Intangible Assets | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 |
| Long-Term Investments | $15.13M | $10.18M | $38.87M | $200.56M | $391.91M | $46.81M | $103.78M | $150.82M | $15.62M | $69.41M | $102.53M | $303K | $303K |
| Deferred Tax Assets | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 |
| Other Long-Term Assets | $4.61M | $6.5M | $7.54M | $9.93M | $10.72M | $9.88M | $10.04M | $26.38M | $1.09M | $625K | $168K | $157K | $0 |
| Total Long-Term Assets | $171.75M | $187.99M | $239M | $417.29M | $595.08M | $176.97M | $152.88M | $205.9M | $30.68M | $79.36M | $103.23M | $460K | $303K |
| Other Assets | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 |
| Total Assets | $453.03M | $465.99M | $573.97M | $833.27M | $1.11B | $708.16M | $497.91M | $543.81M | $198.68M | $172.73M | $221.38M | $3.49M | $2.51M |
| Liabilities | |||||||||||||
| Current Liabilities | |||||||||||||
| Accounts Payable | $21.36M | $22.8M | $22.79M | $27.21M | $11.39M | $10.62M | $6.41M | $4.41M | $4.83M | $1.54M | $1.01M | $334K | $301K |
| Short-Term Debt | $47.9M | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $3.83M | $655K |
| Current Income Tax Payable | $0 | $0 | $0 | $0 | $11.32M | $3.13M | $0 | $726K | $0 | $0 | $0 | $0 | $0 |
| Current Unearned Revenue | $10.45M | $115K | $148K | $1.83M | $3.33M | $449K | $0 | $600K | $0 | $0 | $127K | $153K | -$655K |
| Other Current Liabilities | $20.97M | $51.92M | $86.04M | $66.67M | $57.74M | $51.59M | $10.9M | $6.95M | $3.82M | $4.79M | $1.83M | $153K | $0 |
| Total Current Liabilities | $118.09M | $103.19M | $130.27M | $130.43M | $130.47M | $81.45M | $33.68M | $22.18M | $14.44M | $9.67M | $4.34M | $9.19M | $4.65M |
| Long-Term Liabilities | |||||||||||||
| Long-Term Debt | $147.41M | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 |
| Long-Term Unearned Revenue | $18.94M | $0 | $0 | $0 | $0 | $3.78M | $3.33M | $3.33M | $0 | $0 | $0 | $0 | $0 |
| Long-Term Deferred Tax Liabilities | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $1.1M | $0 | $0 | $0 | $0 | $0 |
| Other Long-Term Liabilities | $638K | $29.01M | $49.73M | $97.84M | $134.21M | $175.03M | $1.83M | $3.6M | $1.21M | $1.33M | $233K | $0 | $0 |
| Total Long-Term Liabilities | $232.2M | $103.14M | $131.96M | $186.64M | $219.13M | $248.96M | $14.04M | $12.79M | $1.21M | $1.33M | $233K | $0 | $0 |
| Other Liabilities | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 |
| Total Liabilities | $350.3M | $206.34M | $262.23M | $317.07M | $349.61M | $330.41M | $47.71M | $34.97M | $15.65M | $10.99M | $4.57M | $9.19M | $4.65M |
| Stockholders' Equity | |||||||||||||
| Preferred Stock | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $12.59M | $11.78M |
| Common Stock | $5K | $5K | $4K | $4K | $4K | $4K | $4K | $4K | $3K | $3K | $3K | $0 | $10.88M |
| Retained Earnings | -$1.13B | -$932.15M | -$705.05M | -$441.55M | -$161.23M | -$289.07M | -$177.82M | -$83.02M | -$187.76M | -$114.59M | -$51.62M | -$28.81M | -$24.81M |
| Comprehensive Income & Other | -$687K | -$741K | -$4.43M | -$15.4M | -$2.57M | -$360K | $205K | -$720K | -$715K | -$33K | -$719K | $0 | $0 |
| Other Stockholders' Equity | $1.23B | $1.19B | $1.02B | $957.74M | $925.53M | $666.82M | $628.01M | $591.86M | $370.78M | $276.32M | $268.43M | $23.11M | $11.78M |
| Total Equity | $102.73M | $259.65M | $311.74M | $516.2M | $764.3M | $377.75M | $450.2M | $508.85M | $183.03M | $161.74M | $216.81M | -$5.7M | -$2.14M |
| Minority Interest | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 |
| Total Liabilities and Equity | $453.03M | $465.99M | $573.97M | $833.27M | $1.11B | $708.16M | $497.91M | $543.81M | $198.68M | $172.73M | $221.38M | $3.49M | $2.51M |
| Supplementary Data | |||||||||||||
| Total Debt | $260.52M | $82.03M | $89.29M | $94.8M | $86.68M | $72.65M | $11.29M | $5.85M | $0 | $0 | $0 | $2.4M | $655K |
| Net Debt | $226.05M | $24.51M | $54.77M | -$2.15M | -$258.53M | -$265.77M | -$58.22M | -$69.71M | -$46.66M | -$24.84M | -$54.12M | $1.28M | -$464K |
| Period | FY 2025 | FY 2024 | FY 2023 | FY 2022 | FY 2021 | FY 2020 | FY 2019 | FY 2018 | FY 2017 | FY 2016 | FY 2015 | FY 2014 | FY 2013 |
|---|---|---|---|---|---|---|---|---|---|---|---|---|---|
| Currency | USD | USD | USD | USD | USD | USD | USD | USD | USD | USD | USD | USD | USD |
| Period Ending | 2025-12-31 | 2024-12-31 | 2023-12-31 | 2022-12-31 | 2021-12-31 | 2020-12-31 | 2019-12-31 | 2018-12-31 | 2017-12-31 | 2016-12-31 | 2015-12-31 | 2014-12-31 | 2013-12-31 |
| Operating Activities | |||||||||||||
| Net Income | -$193.88M | -$227.1M | -$263.49M | -$280.32M | $127.84M | -$111.25M | -$94.73M | $99.94M | -$73.17M | -$62.97M | -$22.81M | -$4M | -$5.39M |
| Depreciation & Amortization | $15.62M | $16.21M | $17.32M | $12.91M | $9.56M | $8.41M | $7.15M | $3.98M | $2.69M | $544K | $80K | $3.68M | $4.76M |
| Deferred Income Tax | $0 | $0 | $0 | $0 | -$1.92M | $3.84M | -$38.97M | $794K | $1.34M | $2M | $322K | $0 | $0 |
| Stock-Based Compensation | $34.56M | $38.46M | $40.27M | $40.79M | $38.81M | $31.95M | $26.85M | $16.64M | $10.61M | $7.03M | $2.92M | $319K | $0 |
| Changes in Working Capital: | |||||||||||||
| Accounts Receivable | -$7.66M | $9.71M | $3.94M | $4.82M | $14.12M | -$9.9M | -$8.62M | -$16.8M | $561K | $1.07M | -$1.34M | -$799K | -$36K |
| Inventory | $0 | $0 | $0 | $0 | $29.3M | $17.85M | $2.37M | $5.35M | -$2.2M | $2.82M | -$2.51M | $1.72M | $4.89M |
| Accounts Payable | -$2.28M | -$292K | -$2.79M | $18.79M | -$2.3M | $3.87M | $1.53M | -$218K | $2.62M | $186K | $590K | $33K | $257K |
| Other Working Capital | $21.73M | -$3.88M | -$12.03M | -$9.63M | -$899K | $2.39M | -$600K | $3.9M | -$86K | $1.15M | $220K | $153K | -$2.45M |
| Total Working Capital Change | $11.78M | $5.53M | -$10.89M | $13.98M | $40.22M | $14.22M | -$5.33M | -$7.77M | $897K | $5.23M | -$3.04M | $1.11M | $2.66M |
| Other Non-Cash Items | $7.96M | -$6.23M | -$1.61M | $5.16M | $4.36M | -$1.23M | -$2.68M | -$8.93M | -$347K | -$399K | $13K | -$3.51M | -$5.05M |
| Net Cash from Operating | -$123.96M | -$173.13M | -$218.41M | -$207.49M | $218.88M | -$54.06M | -$107.7M | $104.65M | -$57.99M | -$48.56M | -$22.52M | -$2.4M | -$3.01M |
| Investing Activities | |||||||||||||
| Capital Expenditures | -$2.41M | -$2.44M | -$9.96M | -$30.72M | -$84.17M | -$26.87M | -$11.72M | -$13.28M | -$7.16M | -$8.15M | -$522K | $0 | $0 |
| Acquisitions | $0 | $0 | $0 | $0 | -$4.99M | -$149.63M | -$295.98M | -$179.71M | -$479K | $0 | $0 | $0 | $0 |
| Purchases of Investments | -$332.63M | -$190.14M | -$86.56M | -$184.88M | -$498.14M | -$123.04M | -$190.74M | -$445.83M | -$68.63M | -$45.07M | -$163.28M | $0 | $0 |
| Sales of Investments | $319.11M | $290.24M | $287.47M | $203.67M | $175.68M | $272.67M | $296.01M | $179.75M | $71M | $72.61M | $0 | $0 | $0 |
| Other Investing Activities | $62K | $5.78M | $0 | $0 | $4.99M | $149.63M | $295.98M | $179.71M | $479K | -$225K | -$163.28M | $0 | $0 |
| Net Cash from Investing | -$15.87M | $103.45M | $190.94M | -$11.93M | -$406.64M | $122.76M | $93.56M | -$279.36M | -$4.79M | $19.16M | -$163.8M | $0 | $0 |
| Financing Activities | |||||||||||||
| Debt Repaid | - | - | - | - | - | - | - | - | - | - | - | - | - |
| Common Stock Issuance | $1.01M | $131.07M | $6.7M | $1.74M | $218.21M | $1.8M | $1.31M | $190.56M | $82.55M | $119K | $145.18M | $0 | $0 |
| Common Stock Repurchases | $0 | $1.19M | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 |
| Dividends Paid | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 |
| Other Financing Activities | $115.76M | -$39.58M | -$41.67M | -$30.58M | -$22.96M | $198.41M | $7.06M | $13.88M | $2.05M | $119K | $107K | $1K | $0 |
| Net Cash from Financing | $116.77M | $92.68M | -$34.97M | -$28.84M | $195.25M | $200.21M | $8.38M | $204.44M | $84.6M | $119K | $239.31M | $2.4M | $1.97M |
| Forex Effect | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 | $0 |
| Net Change in Cash | -$23.06M | $23M | -$62.43M | -$248.26M | $7.48M | $268.91M | -$5.77M | $29.73M | $21.82M | -$29.28M | $52.99M | $2K | -$1.05M |
| Supplementary Data | |||||||||||||
| Operating Cash Flow | -$123.96M | -$173.13M | -$218.41M | -$207.49M | $218.88M | -$54.06M | -$107.7M | $104.65M | -$57.99M | -$48.56M | -$22.52M | -$2.4M | -$3.01M |
| Capital Expenditure | -$2.41M | -$2.44M | -$9.96M | -$30.72M | -$84.17M | -$26.87M | -$11.72M | -$13.28M | -$7.16M | -$8.15M | -$522K | $0 | $0 |
| Free Cash Flow | -$126.38M | -$175.56M | -$228.37M | -$238.21M | $134.7M | -$80.93M | -$119.42M | $91.37M | -$65.15M | -$56.71M | -$23.04M | -$2.4M | -$3.01M |
| Cash at Beginning | $59.56M | $36.55M | $98.98M | $347.24M | $339.76M | $70.84M | $76.61M | $46.88M | $24.84M | $54.12M | $1.12M | $1.12M | $2.17M |
| Cash at End | $36.5M | $59.56M | $36.55M | $98.98M | $347.24M | $339.76M | $70.84M | $76.61M | $46.66M | $24.84M | $54.12M | $1.12M | $1.12M |